RNA Modulation Technology

Amylon’s drug development platform is based on our innovative RNA Modulation Technology. RNA Modulation Technology uses antisense oligonucleotides (ASOs) to alter the splicing of pre-mRNA to counteract the effects of disease-causing mutations.

Amylon Therapeutics

Amylon Therapeutics is a biotechnology company dedicated to developing therapies for rare genetic disorders of the central nervous system. Amylon is led by a strong management team of entrepreneurs and industry veterans, complemented by a world-class supervisory- and scientific advisory board.


Amylon has several therapeutic programs in its pipeline. Our lead research program targets the disorder Hereditary Cerebral Hemorrhage with Amyloidosis Dutch Type (HCHWA-D), also referred to as Katwijk’s disease, the most common form of hereditary cerebral amyloid angiopathy (CAA).

Our Mission

Deliver on the potential of our RNA Modulation Technology by developing life-changing therapeutic solutions for patients with serious unmet medical need.

Press Releases

Dan Curtis joins Amylon Therapeutics as Chief Development Officer

Cambridge, Massachusetts, 26 June 2018  Amylon Therapeutics, a biotechnology company using an ultragenetics approach towards neurological disorders, announces the appointment of Daniel Curtis PhD as its new Chief Development Officer. In his role, Dan will be...

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